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August 21, 2012; 79 (8) Articles

Tafamidis for transthyretin familial amyloid polyneuropathy

A randomized, controlled trial

Teresa Coelho, Luis F. Maia, Ana Martins da Silva, Marcia Waddington Cruz, Violaine Planté-Bordeneuve, Pierre Lozeron, Ole B. Suhr, Josep M. Campistol, Isabel Maria Conceição, Hartmut H.-J. Schmidt, Pedro Trigo, Jeffery W. Kelly, Richard Labaudinière, Jason Chan, Jeff Packman, Amy Wilson, Donna R. Grogan
First published July 25, 2012, DOI: https://doi.org/10.1212/WNL.0b013e3182661eb1
Teresa Coelho
From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa Maria (I.C.), Lisbon, Portugal; Universitatsklinikum Münster (H.H.-J.S.), Münster, Germany; Fundación para la Lucha contra las Enfermedades Neurológicas de la Infancia (FLENI) (P.T.), Buenos Aires, Argentina; The Scripps Research Institute (J.W.K.), La Jolla, CA; Pfizer (R.L., J.P., A.W., D.R.G.), Cambridge, MA; and Kinetic Concepts, Inc. (J.C.), San Antonio, TX.
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Luis F. Maia
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Ana Martins da Silva
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Pierre Lozeron
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Ole B. Suhr
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Josep M. Campistol
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Isabel Maria Conceição
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Hartmut H.-J. Schmidt
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Pedro Trigo
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Jeffery W. Kelly
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Richard Labaudinière
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Jason Chan
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Jeff Packman
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Amy Wilson
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Donna R. Grogan
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Full PDF
Citation
Tafamidis for transthyretin familial amyloid polyneuropathy
A randomized, controlled trial
Teresa Coelho, Luis F. Maia, Ana Martins da Silva, Marcia Waddington Cruz, Violaine Planté-Bordeneuve, Pierre Lozeron, Ole B. Suhr, Josep M. Campistol, Isabel Maria Conceição, Hartmut H.-J. Schmidt, Pedro Trigo, Jeffery W. Kelly, Richard Labaudinière, Jason Chan, Jeff Packman, Amy Wilson, Donna R. Grogan
Neurology Aug 2012, 79 (8) 785-792; DOI: 10.1212/WNL.0b013e3182661eb1

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Letters: Rapid online correspondence

  • Response to Merkies
    • Teresa Coelho, Medical Director, Unidade Clinica de Paramiloidose,[email protected]
    • Joseph C Cappelleri, Michelle Stewart, Pedro E Huertas, Susanne Vidot
    Submitted July 10, 2013
  • Proper outcome measures evaluation in FAP should precede interventional trials
    • Ingemar S.J. Merkies, neurologist and clinimetrician, Maastricht University Medical Centre and Spaarne Hosptial / Corresponding address: Dept Neurology -[email protected]
    Submitted September 07, 2012
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