Drisapersen associated with elevated serum factor VIII levels in Duchenne muscular dystrophy
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Article Information
- Received November 12, 2019
- Accepted in final form January 14, 2020
- First Published February 19, 2020.
Article Versions
- Previous version (February 19, 2020 - 12:45).
- You are viewing the most recent version of this article.
Author Disclosures
- Hugh J. McMillan, MD, MSc,
- Ali Amid, MD,
- Hernan Gonorazky, MD,
- Sulaiman Almobarak, MD and
- Craig Campbell, MD, MSc
- Hugh J. McMillan, MD, MSc,
(1) AveXis (2) Muscular Dystrophy Canada (non-profit entity)
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(1) Muscle Nerve, Editorial Board Member (2016-present); (2) Journal Child Neurology, Editorial Board Member (2011- present)
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Principal Investigator for clinical trials with Sarepta Therapeutics
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- Ali Amid, MD,
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Travel grants for scientific meetings by Novo Nordisk and Octa Pharma. Speaker honororia by Takeda.
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- Hernan Gonorazky, MD,
(1) Serving on a scientific advisory board for Novartis and Biogen
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- Sulaiman Almobarak, MD and
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- Craig Campbell, MD, MSc
(1) Catabasis and Solid Therapeutics DSMB, (2) PTC Therapeutics, Roche and Biogen Scientific Advisory Board Chair (volunteer)
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(1) Valerion Pharmaceuticals (2)PTC Therapeutics (3) Biogen , (4) GEnzyme. Investigator initiated grants. (5) Site investigator for clinical trials: Acceleron, Biogen, Biomarin, AMO, Catabasis, Cytokinetics, GSK, Prosensa, Pfizer, PTC, Roche, Sarepta, Wave.
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(1) Child Health Foundation (2) Jesse's Journey Foundation
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- From the Department of Pediatrics (H.J.M., A.A.), Children's Hospital of Eastern Ontario Research Institute, University of Ottawa, Ottawa; Department of Pediatrics (H.G.), Sick Kids Hospital, University of Toronto, Toronto; and Department of Pediatrics (S.A., C.C.), London Children's Hospital, University of Western Ontario, London, Ontario, Canada.
- Correspondence
Dr. McMillan hmcmillan{at}cheo.on.ca
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