Chiriboga, Claudia et al "Preliminary Evidence for Pharmacodynamics Effects of RG7916 in JEWELFISH, a Study in Patients with Spinal Muscular Atrophy who Previously Participated in a Study with Another SMN2-Splicing Targeting Therapy (S46.003)." Neurology 90.15 Supplement (2018): S46.003. Web. 28 Nov. 2022.